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LTβR Genetics Drisapersen Flavonoid Differentiation Fibroblast Neuromuscular disease KLF15 Dystrophin Gut microbiota Atrial cardiac defects Autophagosome Cell-penetrating peptide Exon Skipping ITSN1 Human muscle stem/progenitor cells Computer software Fear response Cell Therapy Gene Therapy Actin DsDNA break repair Exon skipping CRISPR/Cas9 Chromatin Allele-specific silencing Skeletal muscle DMD Bioinformatics Exondys 51 Lamin A/C nuclei Centronuclear myopathy Autophagy Alternative splicing Myotonic dystrophy RNA interference Canine X-linked muscular dystrophy in Japan CXMD J Exon-skipping Myogenesis Acetylcholine receptor subunit epsilon Insulin Immortalized dystrophic canine myoblast Muscular dystrophy Folding-defective proteins Antisense morpholino Endocytosis CMS Expanded repeats 3D co-culture Duchenne muscular dystrophy Emerin Conjugation HDMD/Dmd-null mice CXCR4 Gene therapy Antisense oligonucleotide Muscle CLS Fluorescence microscopy LRP4 Dominant centronuclear myopathy FoxO Migration Dynamin 2 Glucocorticoid-induced muscle atrophy ICU-acquired weakness Neuromuscular junction Culture platform Immortalisation Developmental biology Eteplirsen Gel electrophoresis DNM2 Myotube DiPRO1 Cell biology CTG⋅CAGn repeat Glucose CXCL12 Human CDNA synthesis Motor neuron BMD Gene network analysis Allele-specific silencing therapy Biomimetism Human artificial chromosomes BAF CFTR correctors Coculture Clinical trial candidate screening Fibrosis Adhesion DM1 myoblasts Duchenne Muscular Dystrophy Becker muscular dystrophy BMD Duchenne muscular dystrophy DMD miRNA nNOS Becker muscular dystrophy Adeno-associated viral vector Bile acid FSHD